Intracerebral administration of rAAV2/5hNAGLU vector in children with MPS IIIB: results at 30 months of a phase I/II trial
Tardieu, Marc, Zerah, Michel, Gougeon, Marie-Lise, Ausseil, Jerome, de Bournonville, Stephanie, Husson, Beatrice, Zafeiriou, Dimitrios, Parenti, GianCarlo, Bourget, Philippe, Artaud, Cecile, Poirier,Volume:
120
Langue:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2016.11.341
Date:
January, 2017
Fichier:
PDF, 48 KB
english, 2017