Volume 26; Issue 2

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Human Gene Therapy
Volume 26; Issue 2

Human Gene Therapy

Volume 26; Issue 2

1

Targeted Oncolytic Herpes Simplex Virus Type 1 Eradicates Experimental Pancreatic Tumors

Gayral, Marion, Lulka, Hubert, Hanoun, Naima, Biollay, Coline, Sèlves, Janick, Vignolle-Vidoni, Alix, Berthommé, Hervé, Trempat, Pascal, Epstein, Alberto L., Buscail, Louis, Béjot, Jean-Luc, Cordelier

Journal:

Human Gene Therapy

Année:

2015

Langue:

english

Fichier:

PDF, 1.02 MB

english, 2015

2

Fanconi Anemia Gene Editing by the CRISPR/Cas9 System

Osborn, Mark J., Gabriel, Richard, Webber, Beau R., DeFeo, Anthony P., McElroy, Amber N., Jarjour, Jordan, Starker, Colby G., Wagner, John E., Joung, J. Keith, Voytas, Daniel F., von Kalle, Christof,

Journal:

Human Gene Therapy

Année:

2015

Langue:

english

Fichier:

PDF, 1.73 MB

english, 2015

3

Intravenous Administration of Retroviral Replicating Vector, Toca 511, Demonstrates Therapeutic Efficacy in Orthotopic Immune-Competent Mouse Glioma Model

Huang, Tiffany T., Parab, Shraddha, Burnett, Ryan, Diago, Oscar, Ostertag, Derek, Hofman, Florence M., Espinoza, Fernando Lopez, Martin, Bryan, Ibañez, Carlos E., Kasahara, Noriyuki, Gruber, Harry E.,

Journal:

Human Gene Therapy

Année:

2015

Langue:

english

Fichier:

PDF, 793 KB

english, 2015

4

Preferential Targeting of Disseminated Liver Tumors Using a Recombinant Adeno-Associated Viral Vector

Della Peruta, Marco, Badar, Adam, Rosales, Cecilia, Chokshi, Shilpa, Kia, Azadeh, Nathwani, Devhrut, Galante, Eva, Yan, Ran, Arstad, Erik, Davidoff, Andrew M., Williams, Roger, Lythgoe, Mark F., Nathw

Journal:

Human Gene Therapy

Année:

2015

Langue:

english

Fichier:

PDF, 900 KB

english, 2015

5

Employing a Gain-of-Function Factor IX Variant R338L to Advance the Efficacy and Safety of Hemophilia B Human Gene Therapy: Preclinical Evaluation Supporting an Ongoing Adeno-Associated Virus Clinical Trial

Monahan, Paul E., Sun, Junjiang, Gui, Tong, Hu, Genlin, Hannah, William B., Wichlan, David G., Wu, Zhijian, Grieger, Joshua C., Li, Chengwen, Suwanmanee, Thipparat, Stafford, Darrel W., Booth, Carmen

Journal:

Human Gene Therapy

Année:

2015

Langue:

english

Fichier:

PDF, 893 KB

english, 2015