Volume 24; Issue 5

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Human Gene Therapy
Volume 24; Issue 5

Human Gene Therapy

Volume 24; Issue 5

1

Antisense Oligonucleotides for the Treatment of Spinal Muscular Atrophy

Porensky, Paul N., Burghes, Arthur H.M.

Journal:

Human Gene Therapy

Année:

2013

Langue:

english

Fichier:

PDF, 388 KB

english, 2013

2

Efficacy of DNA Vaccines Forming E7 Recombinant Retroviral Virus-Like Particles for the Treatment of Human Papillomavirus-Induced Cancers

Lescaille, Geraldine, Pitoiset, Fabien, Macedo, Rodney, Baillou, Claude, Huret, Christophe, Klatzmann, David, Tartour, Eric, Lemoine, François M., Bellier, Bertrand

Journal:

Human Gene Therapy

Année:

2013

Langue:

english

Fichier:

PDF, 750 KB

english, 2013

3

From Mutation Identification to Therapy: Discovery and Origins of the First Approved Gene Therapy in the Western World

Kastelein, John J.P., Ross, Colin J.D., Hayden, Michael R.

Journal:

Human Gene Therapy

Année:

2013

Langue:

english

Fichier:

PDF, 274 KB

english, 2013

4

Antisense Oligonucleotides for Therapeutic Interventions in Neuromuscular Diseases

Journal:

Human Gene Therapy

Année:

2013

Langue:

english

Fichier:

PDF, 52 KB

english, 2013

5

Clinical Trials Using Antisense Oligonucleotides in Duchenne Muscular Dystrophy

Koo, Taeyoung, Wood, Matthew J.

Journal:

Human Gene Therapy

Année:

2013

Langue:

english

Fichier:

PDF, 220 KB

english, 2013

6

Antisense Oligonucleotides: Rising Stars in Eliminating RNA Toxicity in Myotonic Dystrophy

Gao, Zhihua, Cooper, Thomas A.

Journal:

Human Gene Therapy

Année:

2013

Langue:

english

Fichier:

PDF, 268 KB

english, 2013

7

Kinetics of Adeno-Associated Virus Serotype 2 (AAV2) and AAV8 Capsid Antigen Presentation In Vivo Are Identical

He, Yi, Weinberg, Marc S., Hirsch, Matt, Johnson, Mark C., Tisch, Roland, Samulski, R. Jude, Li, Chengwen

Journal:

Human Gene Therapy

Année:

2013

Langue:

english

Fichier:

PDF, 466 KB

english, 2013

8

A Novel Armed Oncolytic Measles Vaccine Virus for the Treatment of Cholangiocarcinoma

Lange, Sebastian, Lampe, Johanna, Bossow, Sascha, Zimmermann, Martina, Neubert, Wolfgang, Bitzer, Michael, Lauer, Ulrich M.

Journal:

Human Gene Therapy

Année:

2013

Langue:

english

Fichier:

PDF, 699 KB

english, 2013

9

British Society for Gene and Cell Therapy (BSGCT) Conference Abstracts Royal Holloway University of London 17–19 April, 2013

Journal:

Human Gene Therapy

Année:

2013

Langue:

english

Fichier:

PDF, 529 KB

english, 2013

10

Strong Cortical and Spinal Cord Transduction After AAV7 and AAV9 Delivery into the Cerebrospinal Fluid of Nonhuman Primates

Samaranch, Lluis, Salegio, Ernesto A., San Sebastian, Waldy, Kells, Adrian P., Bringas, John R., Forsayeth, John, Bankiewicz, Krystof S.

Journal:

Human Gene Therapy

Année:

2013

Langue:

english

Fichier:

PDF, 1.44 MB

english, 2013

11

Gene Therapy Briefs

Philippidis, Alex

Journal:

Human Gene Therapy

Année:

2013

Langue:

english

Fichier:

PDF, 74 KB

english, 2013

12

Hepatic Stellate Cell–Targeted Delivery of Hepatocyte Growth Factor Transgene via Bile Duct Infusion Enhances Its Expression at Fibrotic Foci to Regress Dimethylnitrosamine-Induced Liver Fibrosis

Narmada, Balakrishnan Chakrapani, Kang, Yuzhan, Venkatraman, Lakshmi, Peng, Qiwen, Sakban, Rashidah Binte, Nugraha, Bramasta, Jiang, Xuan, Bunte, Ralph M., So, Peter T.C., Tucker-Kellogg, Lisa, Mao, H

Journal:

Human Gene Therapy

Année:

2013

Langue:

english

Fichier:

PDF, 1.40 MB

english, 2013

13

Recombinant Adeno-Associated Virus Integration Sites in Murine Liver After Ornithine Transcarbamylase Gene Correction

Zhong, Li, Malani, Nirav, Li, Mengxin, Brady, Troy, Xie, Jun, Bell, Peter, Li, Shaoyong, Jones, Haven, Wilson, James M., Flotte, Terence R., Bushman, Frederic D., Gao, Guangping

Journal:

Human Gene Therapy

Année:

2013

Langue:

english

Fichier:

PDF, 437 KB

english, 2013