Volume 23; Issue 8

Main
Human Gene Therapy
Volume 23; Issue 8

Human Gene Therapy

Volume 23; Issue 8

1

Efficacy of Codelivery of Dual AAV2/5 Vectors in the Murine Retina and Hippocampus

Palfi, Arpad, Chadderton, Naomi, McKee, Alex G., Blanco Fernandez, Alfonso, Humphries, Peter, Kenna, Paul F., Farrar, G. Jane

Journal:

Human Gene Therapy

Année:

2012

Langue:

english

Fichier:

PDF, 1.68 MB

english, 2012

2

Inhibition of CD44 Gene Expression in Human Skin Models, Using Self-Delivery Short Interfering RNA Administered by Dissolvable Microneedle Arrays

Lara, Maria Fernanda, González-González, Emilio, Speaker, Tycho J., Hickerson, Robyn P., Leake, Devin, Milstone, Leonard M., Contag, Christopher H., Kaspar, Roger L.

Journal:

Human Gene Therapy

Année:

2012

Langue:

english

Fichier:

PDF, 608 KB

english, 2012

3

Transcription Activator-Like Effector Proteins Induce the Expression of the Frataxin Gene

Tremblay, Jacques P., Chapdelaine, Pierre, Coulombe, Zoé, Rousseau, Joel

Journal:

Human Gene Therapy

Année:

2012

Langue:

english

Fichier:

PDF, 325 KB

english, 2012

4

Gene Therapy of Inherited Retinopathies: A Long and Successful Road from Viral Vectors to Patients

Colella, Pasqualina, Auricchio, Alberto

Journal:

Human Gene Therapy

Année:

2012

Langue:

english

Fichier:

PDF, 300 KB

english, 2012

5

Gene Therapy Approaches for Lysosomal Storage Disease: Next-Generation Treatment

Byrne, Barry J., Falk, Darin J., Clément, Nathalie, Mah, Cathryn S.

Journal:

Human Gene Therapy

Année:

2012

Langue:

english

Fichier:

PDF, 240 KB

english, 2012

6

Systemic Delivery of Oncolytic Adenoviruses Targeting Transforming Growth Factor-β Inhibits Established Bone Metastasis in a Prostate Cancer Mouse Model

Hu, Zebin, Gupta, Janhavi, Zhang, Zhenwei, Gerseny, Helen, Berg, Arthur, Chen, Yun Ju, Zhang, Zhiling, Du, Hongyan, Brendler, Charles B., Xiao, Xianghui, Pienta, Kenneth J., Guise, Theresa, Lee, Chung

Journal:

Human Gene Therapy

Année:

2012

Langue:

english

Fichier:

PDF, 1.38 MB

english, 2012

7

Safety Study of Adeno-Associated Virus Serotype 2-Mediated Human Acid Sphingomyelinase Expression in the Nonhuman Primate Brain

Salegio, Ernesto A., Samaranch, Lluis, Jenkins, Russell W., Clarke, Christopher J., Lamarre, Clementine, Beyer, Janine, Kells, Adrian P., Bringas, John, Sebastian, Waldy San, Richardson, R. Mark, Rose

Journal:

Human Gene Therapy

Année:

2012

Langue:

english

Fichier:

PDF, 1.39 MB

english, 2012

8

Gene Therapy Briefs

Philippidis, Alex

Journal:

Human Gene Therapy

Année:

2012

Langue:

english

Fichier:

PDF, 48 KB

english, 2012

9

Parvalbumin Gene Transfer Impairs Skeletal Muscle Contractility in Old Mice

Murphy, Kate T., Ham, Daniel J., Church, Jarrod E., Naim, Timur, Trieu, Jennifer, Williams, David A., Lynch, Gordon S.

Journal:

Human Gene Therapy

Année:

2012

Langue:

english

Fichier:

PDF, 1003 KB

english, 2012

10

Gene Delivery Improvement for Treating the Lysosomal Storage Disorder Metachromatic Leukodystrophy

Ferraiuolo, Laura, Kaspar, Brian K.

Journal:

Human Gene Therapy

Année:

2012

Langue:

english

Fichier:

PDF, 67 KB

english, 2012

11

Combination of Caspy2 and IP-10 Gene Therapy Significantly Improves Therapeutic Efficacy Against Murine Malignant Neoplasm Growth and Metastasis

Zhang, Na, Yang, Yang, Cheng, Lin, Zhang, Xiao-mei, Zhang, Shuang, Wang, Wei, Liu, Sheng-yong, Wang, Shu-ya, Wang, Rui-bo, Xu, Wen-jing, Dai, Lei, Yan, Nv, Fan, Ping, Dai, Li-xia, Tian, Hong-wei, Liu,

Journal:

Human Gene Therapy

Année:

2012

Langue:

english

Fichier:

PDF, 1.07 MB

english, 2012

12

Tissue Kallikrein Promotes Cardiac Neovascularization by Enhancing Endothelial Progenitor Cell Functional Capacity

Yao, Yuyu, Sheng, Zulong, Li, Yefei, Yan, Fengdi, Fu, Cong, Li, Yongjun, Ma, Genshan, Liu, Naifeng, Chao, Julie, Chao, Lee

Journal:

Human Gene Therapy

Année:

2012

Langue:

english

Fichier:

PDF, 1.39 MB

english, 2012

13

Correction of Brain Oligodendrocytes by AAVrh.10 Intracerebral Gene Therapy in Metachromatic Leukodystrophy Mice

Piguet, Françoise, Sondhi, Dolan, Piraud, Monique, Fouquet, Françoise, Hackett, Neil R., Ahouansou, Ornella, Vanier, Marie-Thérèse, Bieche, Ivan, Aubourg, Patrick, Crystal, Ronald G., Cartier, Nathali

Journal:

Human Gene Therapy

Année:

2012

Langue:

english

Fichier:

PDF, 792 KB

english, 2012