Volume 23; Issue 1

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Human Gene Therapy
Volume 23; Issue 1

Human Gene Therapy

Volume 23; Issue 1

1

The New Self-Inactivating Lentiviral Vector for Thalassemia Gene Therapy Combining Two HPFH Activating Elements Corrects Human Thalassemic Hematopoietic Stem Cells

Papanikolaou, Eleni, Georgomanoli, Maria, Stamateris, Evangelos, Panetsos, Fottes, Karagiorga, Markisia, Tsaftaridis, Panagiotis, Graphakos, Stelios, Anagnou, Nicholas P.

Journal:

Human Gene Therapy

Année:

2012

Langue:

english

Fichier:

PDF, 1.33 MB

english, 2012

2

Efficient Generation of A9 Midbrain Dopaminergic Neurons by Lentiviral Delivery of LMX1A in Human Embryonic Stem Cells and Induced Pluripotent Stem Cells

Sánchez-Danés, A., Consiglio, A., Richaud, Y., Rodríguez-Pizà, I., Dehay, B., Edel, M., Bové, J., Memo, M., Vila, M., Raya, A., Izpisua Belmonte, J.C.

Journal:

Human Gene Therapy

Année:

2012

Langue:

english

Fichier:

PDF, 2.65 MB

english, 2012

3

It's Time for Gene Therapy to Get Disruptive!

Wilson, James M.

Journal:

Human Gene Therapy

Année:

2012

Langue:

english

Fichier:

PDF, 87 KB

english, 2012

4

The European Hospital Exemption Clause—New Option for Gene Therapy?

Buchholz, Christian J., Sanzenbacher, Ralf, Schüle, Silke

Journal:

Human Gene Therapy

Année:

2012

Langue:

english

Fichier:

PDF, 247 KB

english, 2012

5

Novel Mini–Dystrophin Gene Dual Adeno-Associated Virus Vectors Restore Neuronal Nitric Oxide Synthase Expression at the Sarcolemma

Zhang, Yadong, Duan, Dongsheng

Journal:

Human Gene Therapy

Année:

2012

Langue:

english

Fichier:

PDF, 312 KB

english, 2012

6

Distribution Properties of Lentiviral Vectors Administered into the Striatum by Convection-Enhanced Delivery

White, Edward, Bienemann, Alison, Megraw, Lisa, Bunnun, Chotirote, Wyatt, Marcella, Taylor, Hannah, Gill, Steven

Journal:

Human Gene Therapy

Année:

2012

Langue:

english

Fichier:

PDF, 1.92 MB

english, 2012

7

Native Molecular State of Adeno-Associated Viral Vectors Revealed by Single-Molecule Sequencing

Kapranov, Philipp, Chen, Lingxia, Dederich, Debra, Dong, Biao, He, Jie, Steinmann, Kathleen E., Moore, Andrea R., Thompson, John F., Milos, Patrice M., Xiao, Weidong

Journal:

Human Gene Therapy

Année:

2012

Langue:

english

Fichier:

PDF, 533 KB

english, 2012

8

Inactivation of Transcription Factor Pit-1 to Target Tumoral Somatolactotroph Cells

Roche, Catherine, RasolonJanahary, Ramahefarizo, Thirion, Sylvie, Goddard, Isabelle, Fusco, Alexandra, Figarella-Branger, Dominique, Dufour, Henry, Brue, Thierry, Franc, Jean-Louis, Enjalbert, Alain,

Journal:

Human Gene Therapy

Année:

2012

Langue:

english

Fichier:

PDF, 834 KB

english, 2012

9

Response to Intra-Arterial Oncolytic Virotherapy with the Herpes Virus NV1020 Evaluated by [ 18 F]Fluorodeoxyglucose Positron Emission Tomography and Computed Tomography

Sze, Daniel Y., Iagaru, Andrei H., Gambhir, Sanjiv S., De Haan, Hans A., Reid, Tony R.

Journal:

Human Gene Therapy

Année:

2012

Langue:

english

Fichier:

PDF, 423 KB

english, 2012

10

A Potent Oncolytic Adenovirus Selectively Blocks the STAT3 Signaling Pathway and Potentiates Cisplatin Antitumor Activity in Ovarian Cancer

Han, Zhiqiang, Hong, Zhenya, Gao, Qinglei, Chen, Caihong, Hao, Zhou, Ji, Teng, Hu, Wencheng, Yan, Yuting, Feng, Jing, Liao, Shujie, Wu, Peng, Wang, Daowen, Wang, Shixuan, Zhou, Jianfeng, Ma, Ding

Journal:

Human Gene Therapy

Année:

2012

Langue:

english

Fichier:

PDF, 967 KB

english, 2012

11

Gene Therapy Briefs

Philippidis, Alex

Journal:

Human Gene Therapy

Année:

2012

Langue:

english

Fichier:

PDF, 34 KB

english, 2012

12

Hyaluronidase and Collagenase Increase the Transfection Efficiency of Gene Electrotransfer in Various Murine Tumors

Cemazar, Maja, Golzio, Muriel, Sersa, Gregor, Escoffre, Jean-Michel, Coer, Andrej, Vidic, Suzana, Teissie, Justin

Journal:

Human Gene Therapy

Année:

2012

Langue:

english

Fichier:

PDF, 638 KB

english, 2012

13

Human Involucrin Promoter Mediates Repression-Resistant and Compartment-Specific LEKTI Expression

Di, Wei-Li, Semenova, Ekaterina, Larcher, Fernando, Del Rio, Marcela, Harper, John I., Thrasher, Adrian J., Qasim, Waseem

Journal:

Human Gene Therapy

Année:

2012

Langue:

english

Fichier:

PDF, 615 KB

english, 2012

14

Clinical Progress in Gene Therapy: Sustained Partial Correction of the Bleeding Disorder in Patients Suffering from Severe Hemophilia B

VandenDriessche, T., Chuah, M.K.

Journal:

Human Gene Therapy

Année:

2012

Langue:

english

Fichier:

PDF, 77 KB

english, 2012

15

A Transductionally Retargeted Adenoviral Vector for Virotherapy of Her2/neu-Expressing Prostate Cancer

Magnusson, M.K., Kraaij, R., Leadley, R.M., De Ridder, C.M.A., van Weerden, W.M., Van Schie, K.A.J., Van der Kroeg, M., Hoeben, R.C., Maitland, N.J., Lindholm, L.

Journal:

Human Gene Therapy

Année:

2012

Langue:

english

Fichier:

PDF, 986 KB

english, 2012