Volume 22; Issue 2

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Human Gene Therapy
Volume 22; Issue 2

Human Gene Therapy

Volume 22; Issue 2

1

Combination of SMN Trans -Splicing and a Neurotrophic Factor Increases the Life Span and Body Mass in a Severe Model of Spinal Muscular Atrophy

Shababi, Monir, Glascock, Jacqueline, Lorson, Christian L.

Journal:

Human Gene Therapy

Année:

2011

Langue:

english

Fichier:

PDF, 436 KB

english, 2011

2

Retroviral and Transposon-Based Tet-Regulated All-In-One Vectors with Reduced Background Expression and Improved Dynamic Range

Heinz, Niels, Schambach, Axel, Galla, Melanie, Maetzig, Tobias, Baum, Christopher, Loew, Rainer, Schiedlmeier, Bernhard

Journal:

Human Gene Therapy

Année:

2011

Fichier:

PDF, 393 KB

2011

3

Tracking of Specific Integrant Clones in Dogs Treated with Foamy Virus Vectors

Ohmine, Ken, Li, Yi, Bauer, Thomas R., Hickstein, Dennis D., Russell, David W.

Journal:

Human Gene Therapy

Année:

2011

Langue:

english

Fichier:

PDF, 380 KB

english, 2011

4

HIV-1-Derived Lentiviral Vectors Directly Activate Plasmacytoid Dendritic Cells, Which in Turn Induce the Maturation of Myeloid Dendritic Cells

Rossetti, Maura, Gregori, Silvia, Hauben, Ehud, Brown, Brian D., Sergi, Lucia Sergi, Naldini, Luigi, Roncarolo, Maria-Grazia

Journal:

Human Gene Therapy

Année:

2011

Langue:

english

Fichier:

PDF, 888 KB

english, 2011

5

Noninvasive Repetitive Imaging of Somatostatin Receptor 2 Gene Transfer with Positron Emission Tomography

Cotugno, Gabriella, Aurilio, Michela, Annunziata, Patrizia, Capalbo, Anita, Faella, Armida, Rinaldi, Valentina, Strisciuglio, Caterina, Tommaso, Maurizio Di, Aloj, Luigi, Auricchio, Alberto

Journal:

Human Gene Therapy

Année:

2011

Langue:

english

Fichier:

PDF, 455 KB

english, 2011

6

Preclinical Evaluation of a Recombinant Adeno-Associated Virus Vector Expressing Human Alpha-1 Antitrypsin Made Using a Recombinant Herpes Simplex Virus Production Method

Chulay, Jeffrey D., Ye, Guo-Jie, Thomas, Darby L., Knop, David R., Benson, Janet M., Hutt, Julie A., Wang, Gensheng, Humphries, Margaret, Flotte, Terence R.

Journal:

Human Gene Therapy

Année:

2011

Langue:

english

Fichier:

PDF, 534 KB

english, 2011

7

The Wire

Journal:

Human Gene Therapy

Année:

2011

Langue:

english

Fichier:

PDF, 235 KB

english, 2011

8

Trans -Splicing, More Than Meets the Eye: Multifaceted Therapeutics for Spinal Muscular Atrophy

Butchbach, Matthew E.R.

Journal:

Human Gene Therapy

Année:

2011

Langue:

english

Fichier:

PDF, 189 KB

english, 2011

9

Toward a Proportionate Regulatory Framework for Gene Transfer: A Patient Group-Led Initiative

Kent, Alastair, King, Nancy M.P., Cohen-Haguenauer, Odile

Journal:

Human Gene Therapy

Année:

2011

Langue:

english

Fichier:

PDF, 172 KB

english, 2011

10

The Technology of Gene Therapy

Wilson, James M.

Journal:

Human Gene Therapy

Année:

2011

Langue:

english

Fichier:

PDF, 26 KB

english, 2011

11

Muscle Damage After Delivery of Naked Plasmid DNA into Skeletal Muscles Is Batch Dependent

Wooddell, Christine I., Subbotin, Vladimir M., Sebestyén, Magdolna G., Griffin, Jacob B., Zhang, Guofeng, Schleef, Martin, Braun, Serge, Huss, Thierry, Wolff, Jon A.

Journal:

Human Gene Therapy

Année:

2011

Langue:

english

Fichier:

PDF, 723 KB

english, 2011

12

Evaluation and Optimization of the Administration of Recombinant Adeno-Associated Viral Vectors (Serotypes 2/1, 2/2, 2/rh8, 2/9, and 2/rh10) by Convection-Enhanced Delivery to the Striatum

White, Edward, Bienemann, Alison, Sena-Esteves, Miguel, Taylor, Hannah, Bunnun, Chotirote, Castrique, Emma, Gill, Steven

Journal:

Human Gene Therapy

Année:

2011

Langue:

english

Fichier:

PDF, 1.67 MB

english, 2011

13

Postacute Ischemia Vascular Endothelial Growth Factor Transfer by Transferrin-Targeted Liposomes Attenuates Ischemic Brain Injury After Experimental Stroke in Rats

Zhao, Hao, Bao, Xin-jie, Wang, Ren-zhi, Li, Gui-lin, Gao, Jun, Ma, Si-hai, Wei, Jun-ji, Feng, Ming, Zhao, Ying-jie, Ma, Wen-bin, Yang, Yi, Li, Yong-ning, Kong, Yan-guo

Journal:

Human Gene Therapy

Année:

2011

Langue:

english

Fichier:

PDF, 446 KB

english, 2011

14

Amelioration of Rat Collagen-Induced Arthritis Through CD4 + T Cells Apoptosis and Synovial Interleukin-17 Reduction by Indoleamine 2,3-Dioxygenase Gene Therapy

Chen, Shih-Yao, Wu, Chao-Liang, Lai, Ming-Derg, Lin, Chi-Chen, Yo, Yi-Te, Jou, I-Ming, Lee, Che-Hsin, Weng, Chia-Tse, Shiau, Ai-Li, Wang, Chrong-Reen

Journal:

Human Gene Therapy

Année:

2011

Langue:

english

Fichier:

PDF, 826 KB

english, 2011

15

A Lentiviral Strategy for Highly Efficient Retrograde Gene Transfer by Pseudotyping with Fusion Envelope Glycoprotein

Kato, Shigeki, Kobayashi, Kenta, Inoue, Ken-ichi, Kuramochi, Masahito, Okada, Tomoaki, Yaginuma, Hiroyuki, Morimoto, Kinjiro, Shimada, Takashi, Takada, Masahiko, Kobayashi, Kazuto

Journal:

Human Gene Therapy

Année:

2011

Langue:

english

Fichier:

PDF, 640 KB

english, 2011