Volume 12; Issue supp-S

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Neuromuscular Disorders
Volume 12; Issue supp-S

Neuromuscular Disorders

Volume 12; Issue supp-S

1

Foreword

Journal:

Neuromuscular Disorders

Année:

2002

Langue:

english

Fichier:

PDF, 38 KB

english, 2002

2

Myoblast transplantation

Terry Partridge

Journal:

Neuromuscular Disorders

Année:

2002

Langue:

english

Fichier:

PDF, 56 KB

english, 2002

3

Gene transfer studies in animals: what do they really tell us about the prospects for gene therapy in DMD?

Dominic J Wells, Kim E Wells

Journal:

Neuromuscular Disorders

Année:

2002

Langue:

english

Fichier:

PDF, 123 KB

english, 2002

4

Viral vectors for gene transfer of micro-, mini-, or full-length dystrophin

Jeannine M Scott, Sheng Li, Scott Q Harper, Robert Welikson, Daniel Bourque, Christiana DelloRusso, Stephen D Hauschka, Jeffrey S Chamberlain

Journal:

Neuromuscular Disorders

Année:

2002

Langue:

english

Fichier:

PDF, 418 KB

english, 2002

5

Strategies for muscle-specific targeting of adenoviral gene transfer vectors

Christian Thirion, Nancy Larochelle, Christoph Volpers, Patrick Dunant, Rolf Stucka, Paul Holland, Josephine Nalbantoglu, Stefan Kochanek, Hanns Lochmüller

Journal:

Neuromuscular Disorders

Année:

2002

Langue:

english

Fichier:

PDF, 352 KB

english, 2002

6

Recombinant micro-genes and dystrophin viral vectors

G Dickson, M.L Roberts, D.J Wells, S.A Fabb

Journal:

Neuromuscular Disorders

Année:

2002

Langue:

english

Fichier:

PDF, 152 KB

english, 2002

7

Current protocol of a research phase I clinical trial of full-length dystrophin plasmid DNA in Duchenne/Becker muscular dystrophies: Part II: clinical protocol

Norma Beatriz Romero, Olivier Benveniste, Christine Payan, Serge Braun, Patrick Squiban, Serge Herson, Michel Fardeau

Journal:

Neuromuscular Disorders

Année:

2002

Langue:

english

Fichier:

PDF, 115 KB

english, 2002

8

Current protocol of a research phase I clinical trial of full-length dystrophin plasmid DNA in Duchenne/Becker muscular dystrophies: Part I: rationale

Christine Thioudellet, Stéphane Blot, Patrick Squiban, Michel Fardeau, Serge Braun

Journal:

Neuromuscular Disorders

Année:

2002

Langue:

english

Fichier:

PDF, 162 KB

english, 2002

9

Oligonucleotide-mediated gene therapy for muscular dystrophies

Journal:

Neuromuscular Disorders

Année:

2002

Langue:

english

Fichier:

PDF, 78 KB

english, 2002

10

CD45 fraction bone marrow cells as potential delivery vehicles for genetically corrected dystrophin loci

R.M.I Kapsa, S.H.A Wong, I Bertoncello, A.F Quigley, B Williams, K Sells, R Marotta, M Kita, P Simmons, E Byrne, A.J Kornberg

Journal:

Neuromuscular Disorders

Année:

2002

Langue:

english

Fichier:

PDF, 216 KB

english, 2002

11

Screening for antisense modulation of dystrophin pre-mRNA splicing

G Dickson, V Hill, I.R Graham

Journal:

Neuromuscular Disorders

Année:

2002

Langue:

english

Fichier:

PDF, 63 KB

english, 2002

12

Targeted exon skipping as a potential gene correction therapy for Duchenne muscular dystrophy

Annemieke Aartsma-Rus, Mattie Bremmer-Bout, Anneke A.M Janson, Johan T den Dunnen, Gert-Jan B van Ommen, Judith C.T van Deutekom

Journal:

Neuromuscular Disorders

Année:

2002

Langue:

english

Fichier:

PDF, 165 KB

english, 2002

13

The role of utrophin in the potential therapy of Duchenne muscular dystrophy

Kelly J Perkins, Kay E Davies

Journal:

Neuromuscular Disorders

Année:

2002

Langue:

english

Fichier:

PDF, 243 KB

english, 2002

14

Multivariate evaluation of the functional recovery obtained by the overexpression of utrophin in skeletal muscles of the mdx mouse

Jean-Marie Gillis

Journal:

Neuromuscular Disorders

Année:

2002

Langue:

english

Fichier:

PDF, 137 KB

english, 2002

15

Glucocorticoid-mediated regulation of utrophin levels in human muscle fibers

Isabelle Courdier-Fruh, Lee Barman, Alexandre Briguet, Thomas Meier

Journal:

Neuromuscular Disorders

Année:

2002

Langue:

english

Fichier:

PDF, 218 KB

english, 2002

16

Dystrophin and functionally related proteins in the nematode Caenorhabditis elegans

Laurent Ségalat

Journal:

Neuromuscular Disorders

Année:

2002

Langue:

english

Fichier:

PDF, 168 KB

english, 2002

17

Dystrobrevin dynamics in muscle–cell signalling: a possible target for therapeutic intervention in Duchenne muscular dystrophy?

Journal:

Neuromuscular Disorders

Année:

2002

Langue:

english

Fichier:

PDF, 336 KB

english, 2002

18

Expression profiling in stably regenerating skeletal muscle of dystrophin-deficient mdx mice

Judith M. Boer, Emile J. de Meijer, Eveline M. Mank, Gertjan B. van Ommen, Johan T. den Dunnen

Journal:

Neuromuscular Disorders

Année:

2002

Langue:

english

Fichier:

PDF, 82 KB

english, 2002

19

A web-accessible complete transcriptome of normal human and DMD muscle

Marina Bakay, Po Zhao, Josephine Chen, Eric P Hoffman

Journal:

Neuromuscular Disorders

Année:

2002

Langue:

english

Fichier:

PDF, 491 KB

english, 2002

20

Collaborative translational research leading to multicenter clinical trials in Duchenne muscular dystrophy: the Cooperative International Neuromuscular Research Group (CINRG)

Diana M Escolar, Erik K Henricson, Livia Pasquali, Ksenija Gorni, Eric P Hoffman

Journal:

Neuromuscular Disorders

Année:

2002

Langue:

english

Fichier:

PDF, 213 KB

english, 2002

21

Pharmacological control of cellular calcium handling in dystrophic skeletal muscle

Urs T Ruegg, Valérie Nicolas-Métral, Corinne Challet, Katy Bernard-Hélary, Olivier M Dorchies, Stéphanie Wagner, Timo M Buetler

Journal:

Neuromuscular Disorders

Année:

2002

Langue:

english

Fichier:

PDF, 203 KB

english, 2002

22

Considerations to the policy of future clinical therapeutic trials in DMD

Journal:

Neuromuscular Disorders

Année:

2002

Langue:

english

Fichier:

PDF, 96 KB

english, 2002

23

An effective, low-dosage, intermittent schedule of prednisolone in the long-term treatment of early cases of Duchenne dystrophy

Maria Kinali, Eugenio Mercuri, Marion Main, Francesco Muntoni, Victor Dubowitz

Journal:

Neuromuscular Disorders

Année:

2002

Langue:

english

Fichier:

PDF, 171 KB

english, 2002

24

Current protocol of a research phase I clinical trial of full-length dystrophin plasmid DNA in Duchenne/Becker muscular dystrophies: Part III. Ethical considerations

Journal:

Neuromuscular Disorders

Année:

2002

Langue:

english

Fichier:

PDF, 46 KB

english, 2002

25

Pre-clinical trials in Duchenne dystrophy: what animal models can tell us about potential drug effectiveness

Annamaria De Luca, Sabata Pierno, Antonella Liantonio, Diana Conte Camerino

Journal:

Neuromuscular Disorders

Année:

2002

Langue:

english

Fichier:

PDF, 74 KB

english, 2002

26

Steroids in Duchenne muscular dystrophy: from clinical trials to genomic research

Francesco Muntoni, Ivan Fisher, Jennifer E Morgan, David Abraham

Journal:

Neuromuscular Disorders

Année:

2002

Langue:

english

Fichier:

PDF, 60 KB

english, 2002

27

Myogenic stem cells from the bone marrow: a therapeutic alternative for muscular dystrophy?

Giuliana Ferrari, Fulvio Mavilio

Journal:

Neuromuscular Disorders

Année:

2002

Langue:

english

Fichier:

PDF, 61 KB

english, 2002

28

Editorial Board

Journal:

Neuromuscular Disorders

Année:

2002

Langue:

english

Fichier:

PDF, 28 KB

english, 2002