Volume 23; Issue 7

Main
Molecular Therapy
Volume 23; Issue 7

Molecular Therapy

Volume 23; Issue 7

1

Pharmacological Chaperone Therapy: Preclinical Development, Clinical Translation, and Prospects for the Treatment of Lysosomal Storage Disorders

Parenti, Giancarlo, Andria, Generoso, Valenzano, Kenneth J

Journal:

Molecular Therapy

Année:

2015

Langue:

english

Fichier:

PDF, 669 KB

english, 2015

2

Monocyte/Macrophage-derived IGF-1 Orchestrates Murine Skeletal Muscle Regeneration and Modulates Autocrine Polarization

Tonkin, Joanne, Temmerman, Lieve, Sampson, Robert D, Gallego-Colon, Enrique, Barberi, Laura, Bilbao, Daniel, Schneider, Michael D, Musarò, Antonio, Rosenthal, Nadia

Journal:

Molecular Therapy

Année:

2015

Langue:

english

Fichier:

PDF, 2.73 MB

english, 2015

3

Engineering T Cells to Functionally Cure HIV-1 Infection

Leibman, Rachel S, Riley, James L

Journal:

Molecular Therapy

Année:

2015

Langue:

english

Fichier:

PDF, 619 KB

english, 2015

4

The Cancer Genome Atlas Analysis Predicts MicroRNA for Targeting Cancer Growth and Vascularization in Glioblastoma

Wong, Hon-Kit Andus, Fatimy, Rachid El, Onodera, Courtney, Wei, Zhiyun, Yi, Ming, Mohan, Athul, Gowrisankaran, Sindhuja, Karmali, Priya, Marcusson, Eric, Wakimoto, Hiroaki, Stephens, Robert, Uhlmann,

Journal:

Molecular Therapy

Année:

2015

Langue:

english

Fichier:

PDF, 3.95 MB

english, 2015

5

Barrier Function of the Repaired Skin Is Disrupted Following Arrest of Dicer in Keratinocytes

Ghatak, Subhadip, Chan, Yuk Cheung, Khanna, Savita, Banerjee, Jaideep, Weist, Jessica, Roy, Sashwati, Sen, Chandan K

Journal:

Molecular Therapy

Année:

2015

Langue:

english

Fichier:

PDF, 1.36 MB

english, 2015

6

Bioengineering Thymus Organoids to Restore Thymic Function and Induce Donor-Specific Immune Tolerance to Allografts

Fan, Yong, Tajima, Asako, Goh, Saik Kia, Geng, Xuehui, Gualtierotti, Giulio, Grupillo, Maria, Coppola, Antonina, Bertera, Suzanne, Rudert, William A, Banerjee, Ipsita, Bottino, Rita, Trucco, Massimo

Journal:

Molecular Therapy

Année:

2015

Langue:

english

Fichier:

PDF, 3.33 MB

english, 2015

7

Cardiac AAV9 Gene Delivery Strategies in Adult Canines: Assessment by Long-term Serial SPECT Imaging of Sodium Iodide Symporter Expression

Moulay, Gilles, Ohtani, Tomohito, Ogut, Ozgur, Guenzel, Adam, Behfar, Atta, Zakeri, Rosita, Haines, Philip, Storlie, Jimmy, Bowen, Lorna, Pham, Linh, Kaye, David, Sandhu, Gurpreet, O’Connor, Michael,

Journal:

Molecular Therapy

Année:

2015

Langue:

english

Fichier:

PDF, 3.39 MB

english, 2015

8

Mesenchymal Stromal Cells Derived From Crohn’s Patients Deploy Indoleamine 2,3-dioxygenase-mediated Immune Suppression, Independent of Autophagy

Chinnadurai, Raghavan, Copland, Ian B, Ng, Spencer, Garcia, Marco, Prasad, Mahadev, Arafat, Dalia, Gibson, Greg, Kugathasan, Subra, Galipeau, Jacques

Journal:

Molecular Therapy

Année:

2015

Langue:

english

Fichier:

PDF, 3.16 MB

english, 2015

9

Inhibition of Dexamethasone-induced Fatty Liver Development by Reducing miR-17-5p Levels

Du, William W, Liu, Fengqiong, Shan, Sze Wan, Ma, Xindi Cindy, Gupta, Shaan, Jin, Tianru, Spaner, David, Krylov, Sergey N, Zhang, Yaou, Ling, Wenhua, Yang, Burton B

Journal:

Molecular Therapy

Année:

2015

Langue:

english

Fichier:

PDF, 5.05 MB

english, 2015

10

Anti-inflammatory Therapy With Simvastatin Improves Neuroinflammation and CNS Function in a Mouse Model of Metachromatic Leukodystrophy

Stein, Axel, Stroobants, Stijn, Gieselmann, Volkmar, D'Hooge, Rudi, Matzner, Ulrich

Journal:

Molecular Therapy

Année:

2015

Langue:

english

Fichier:

PDF, 3.39 MB

english, 2015

11

Research Highlights

Journal:

Molecular Therapy

Année:

2015

Langue:

english

Fichier:

PDF, 723 KB

english, 2015

12

Oncolytic Treatment for Cancer Recommended for Approval

Journal:

Molecular Therapy

Année:

2015

Langue:

english

Fichier:

PDF, 497 KB

english, 2015

13

Macrophage-Derived IGF-1 Is a Potent Coordinator of Myogenesis and Inflammation in Regenerating Muscle

Tidball, James G, Welc, Steven S

Journal:

Molecular Therapy

Année:

2015

Langue:

english

Fichier:

PDF, 693 KB

english, 2015

14

Coformulation of a Novel Human α-Galactosidase A With the Pharmacological Chaperone AT1001 Leads to Improved Substrate Reduction in Fabry Mice

Xu, Su, Lun, Yi, Brignol, Nastry, Hamler, Rick, Schilling, Adriane, Frascella, Michelle, Sullivan, Sean, Boyd, Robert E, Chang, Kate, Soska, Rebecca, Garcia, Anadina, Feng, Jessie, Yasukawa, Hidehito,

Journal:

Molecular Therapy

Année:

2015

Langue:

english

Fichier:

PDF, 4.40 MB

english, 2015

15

Corrigendum to “Insulin-like Growth Factor-binding Protein-7 (IGFBP7): A Promising Gene Therapeutic for Hepatocellular Carcinoma (HCC)”

Journal:

Molecular Therapy

Année:

2015

Langue:

english

Fichier:

PDF, 397 KB

english, 2015

16

Experimental Curative Fluorescence-guided Surgery of Highly Invasive Glioblastoma Multiforme Selectively Labeled With a Killer-reporter Adenovirus

Yano, Shuya, Miwa, Shinji, Kishimoto, Hiroyuki, Toneri, Makoto, Hiroshima, Yukihiko, Yamamoto, Mako, Bouvet, Michael, Urata, Yasuo, Tazawa, Hiroshi, Kagawa, Shunsuke, Fujiwara, Toshiyoshi, Hoffman, Ro

Journal:

Molecular Therapy

Année:

2015

Langue:

english

Fichier:

PDF, 3.67 MB

english, 2015

17

In This Issue

Journal:

Molecular Therapy

Année:

2015

Langue:

english

Fichier:

PDF, 398 KB

english, 2015

18

Shedding New Light on the Use of Imaging Technology for Glioblastoma Tumor Resection

Nemunaitis, John, Senzer, Neil

Journal:

Molecular Therapy

Année:

2015

Langue:

english

Fichier:

PDF, 693 KB

english, 2015

19

Corrigendum to “Chimeric Receptors Containing CD137 Signal Transduction Domains Mediate Enhanced Survival of T Cells and Increased Antileukemic Efficacy In Vivo”

Journal:

Molecular Therapy

Année:

2015

Langue:

english

Fichier:

PDF, 397 KB

english, 2015