Volume 16; Issue 4

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Molecular Therapy
Volume 16; Issue 4

Molecular Therapy

Volume 16; Issue 4

1

A Multicolor Panel of Novel Lentiviral “Gene Ontology” (LeGO) Vectors for Functional Gene Analysis

Weber, Kristoffer, Bartsch, Udo, Stocking, Carol, Fehse, Boris

Journal:

Molecular Therapy

Année:

2008

Langue:

english

Fichier:

PDF, 1.07 MB

english, 2008

2

Ranibizumab for Macular Edema Due to Retinal Vein Occlusions: Implication of VEGF as a Critical Stimulator

Campochiaro, Peter A, Hafiz, Gulnar, Shah, Syed Mahmood, Nguyen, Quan Dong, Ying, Howard, Do, Diana V, Quinlan, Edward, Zimmer-Galler, Ingrid, Haller, Julia A, Solomon, Sharon D, Sung, Jennifer U, Had

Journal:

Molecular Therapy

Année:

2008

Langue:

english

Fichier:

PDF, 856 KB

english, 2008

3

Comparison of Zinc Finger Nucleases for Use in Gene Targeting in Mammalian Cells

Pruett-Miller, Shondra M, Connelly, Jon P, Maeder, Morgan L, Joung, J Keith, Porteus, Matthew H

Journal:

Molecular Therapy

Année:

2008

Langue:

english

Fichier:

PDF, 336 KB

english, 2008

4

Efficient In Vivo Delivery of siRNA to the Liver by Conjugation of α-Tocopherol

Nishina, Kazutaka, Unno, Toshinori, Uno, Yoshitaka, Kubodera, Takayuki, Kanouchi, Tadashi, Mizusawa, Hidehiro, Yokota, Takanori

Journal:

Molecular Therapy

Année:

2008

Langue:

english

Fichier:

PDF, 355 KB

english, 2008

5

A Tumor-selective Biotherapy With Prolonged Impact on Established Metastases Based on Cytokine Gene-engineered MSCs

Chen, Xiancheng, Lin, Xiaojuan, Zhao, Jianlei, Shi, Wei, Zhang, Heng, Wang, Yongsheng, Kan, Bing, Du, Licheng, Wang, Baiding, Wei, Yuquan, Liu, Yi, Zhao, Xia

Journal:

Molecular Therapy

Année:

2008

Langue:

english

Fichier:

PDF, 816 KB

english, 2008

6

Phase I Clinical Trial of Autologous Ascites-derived Exosomes Combined With GM-CSF for Colorectal Cancer

Dai, Shengming, Wei, Dong, Wu, Zhen, Zhou, Xiangyang, Wei, Xiaomou, Huang, Haixin, Li, Guisheng

Journal:

Molecular Therapy

Année:

2008

Langue:

english

Fichier:

PDF, 232 KB

english, 2008

7

Mechanisms of Immunization Against Cancer Using Chimeric Antigens

Engelhorn, Manuel E, Guevara-Patiño, José A, Merghoub, Taha, Liu, Cailian, Ferrone, Cristina R, Rizzuto, Gabriele A, Cymerman, Daniel H, Posnett, David N, Houghton, Alan N, Wolchok, Jedd D

Journal:

Molecular Therapy

Année:

2008

Langue:

english

Fichier:

PDF, 321 KB

english, 2008

8

Intraventricular Enzyme Replacement Improves Disease Phenotypes in a Mouse Model of Late Infantile Neuronal Ceroid Lipofuscinosis

Chang, Michael, Cooper, Jonathan D, Sleat, David E, Cheng, Seng H, Dodge, James C, Passini, Marco A, Lobel, Peter, Davidson, Beverly L

Journal:

Molecular Therapy

Année:

2008

Langue:

english

Fichier:

PDF, 1.10 MB

english, 2008

9

Systemic Microdystrophin Gene Delivery Improves Skeletal Muscle Structure and Function in Old Dystrophic mdx Mice

Gregorevic, Paul, Blankinship, Michael J, Allen, James M, Chamberlain, Jeffrey S

Journal:

Molecular Therapy

Année:

2008

Fichier:

PDF, 889 KB

2008

10

Transduction Properties of Adenovirus Serotype 35 Vectors After Intravenous Administration Into Nonhuman Primates

Sakurai, Fuminori, Nakamura, Shin-ichiro, Akitomo, Kimiyo, Shibata, Hiroaki, Terao, Keiji, Kawabata, Kenji, Hayakawa, Takao, Mizuguchi, Hiroyuki

Journal:

Molecular Therapy

Année:

2008

Langue:

english

Fichier:

PDF, 654 KB

english, 2008

11

AAV Vector-mediated Reversal of Hypoglycemia in Canine and Murine Glycogen Storage Disease Type Ia

Koeberl, Dwight D, Pinto, Carlos, Sun, Baodong, Li, Songtao, Kozink, Daniel M, Benjamin Jr., Daniel K, Demaster, Amanda K, Kruse, Meghan A, Vaughn, Valerie, Hillman, Steven, Bird, Andrew, Jackson, Mar

Journal:

Molecular Therapy

Année:

2008

Langue:

english

Fichier:

PDF, 388 KB

english, 2008

12

Genetic Complementation of Human Muscle Cells via Directed Stem Cell Fusion

Gonçalves, Manuel AFV, Swildens, Jim, Holkers, Maarten, Narain, Anjali, van Nierop, Gijsbert P, van de Watering, Marloes JM, Knaän-Shanzer, Shoshan, de Vries, Antoine AF

Journal:

Molecular Therapy

Année:

2008

Langue:

english

Fichier:

PDF, 857 KB

english, 2008

13

Systemic Microdystrophin Gene Delivery Improves Skeletal Muscle Structure and Function in Old Dystrophic mdx Mice

Gregorevic, Paul, Blankinship, Michael J, Allen, James M, Chamberlain, Jeffrey S

Journal:

Molecular Therapy

Année:

2008

Langue:

english

Fichier:

PDF, 889 KB

english, 2008

14

Gene Delivery to the Nervous System

Schubert, Manfred, Breakefield, Xandra, Federoff, Howard, Frederickson, Robert M, Lowenstein, Pedro R

Journal:

Molecular Therapy

Année:

2008

Langue:

english

Fichier:

PDF, 292 KB

english, 2008

15

Physiological Promoters Reduce the Genotoxic Risk of Integrating Gene Vectors

Zychlinski, Daniela, Schambach, Axel, Modlich, Ute, Maetzig, Tobias, Meyer, Johann, Grassman, Elke, Mishra, Anjali, Baum, Christopher

Journal:

Molecular Therapy

Année:

2008

Langue:

english

Fichier:

PDF, 391 KB

english, 2008

16

A Comprehensive Platform for Ex Vivo T-cell Expansion Based on Biodegradable Polymeric Artificial Antigen-presenting Cells

Steenblock, Erin R, Fahmy, Tarek M

Journal:

Molecular Therapy

Année:

2008

Langue:

english

Fichier:

PDF, 561 KB

english, 2008

17

Correction of Murine PKU Following AAV-mediated Intramuscular Expression of a Complete Phenylalanine Hydroxylating System

Ding, Zhaobing, Harding, Cary O, Rebuffat, Alexandre, Elzaouk, Lina, Wolff, Jon A, Thöny, Beat

Journal:

Molecular Therapy

Année:

2008

Langue:

english

Fichier:

PDF, 306 KB

english, 2008

18

TAT-mediated Delivery of LAD Restores Pyruvate Dehydrogenase Complex Activity in the Mitochondria of Patients with LAD Deficiency

Rapoport, Matan, Saada, Ann, Elpeleg, Orly, Lorberboum-Galski, Haya

Journal:

Molecular Therapy

Année:

2008

Langue:

english

Fichier:

PDF, 282 KB

english, 2008

19

Foamy Virus Vectors Come of Age

Williams, David A

Journal:

Molecular Therapy

Année:

2008

Langue:

english

Fichier:

PDF, 113 KB

english, 2008

20

TAT Opens the Door

Vyas, Piyush M, Payne, Ronald M

Journal:

Molecular Therapy

Année:

2008

Langue:

english

Fichier:

PDF, 239 KB

english, 2008

21

Flt3L in Combination With HSV1-TK-mediated Gene Therapy Reverses Brain Tumor–induced Behavioral Deficits

King, Gwendalyn D, Kroeger, Kurt M, Bresee, Catherine J, Candolfi, Marianela, Liu, Chunyan, Manalo, Charlene M, Muhammad, AKM Ghulam, Pechnick, Robert N, Lowenstein, Pedro R, Castro, Maria G

Journal:

Molecular Therapy

Année:

2008

Langue:

english

Fichier:

PDF, 531 KB

english, 2008

22

Gene Therapy of βc-Deficient Pulmonary Alveolar Proteinosis (βc-PAP): Studies in a Murine in vivo Model

Kleff, Veronika, Sorg, Ursula R, Bury, Carsten, Suzuki, Takuji, Rattmann, Ina, Jerabek-Willemsen, Moran, Poremba, Christopher, Flasshove, Michael, Opalka, Bertram, Trapnell, Bruce, Dirksen, Uta, Morit

Journal:

Molecular Therapy

Année:

2008

Langue:

english

Fichier:

PDF, 398 KB

english, 2008

23

In This Issue

Journal:

Molecular Therapy

Année:

2008

Fichier:

PDF, 1.36 MB

2008

24

Research Highlights

Journal:

Molecular Therapy

Année:

2008

Fichier:

PDF, 387 KB

2008