
Substrate reduction therapy using Genzâ667161 reduces levels of pathogenic components in a mouse model of neuronopathic forms of Gaucher disease
Blumenreich, Shani, Yaacobi, Chen, Vardi, Ayelet, Barav, Or B., Vitner, Einat B., Park, Hyejung, Wang, Bing, Cheng, Seng H., Sardi, S. Pablo, Futerman, Anthony H.Journal:
Journal of Neurochemistry
DOI:
10.1111/jnc.15136
Date:
August, 2020
Fichier:
PDF, 13.97 MB
2020