Myostatin Is a Quantifiable Biomarker for Monitoring Pharmaco-gene Therapy in Duchenne Muscular Dystrophy
Mariot, Virginie, Le Guiner, Caroline, Barthélémy, Inès, Montus, Marie, Blot, Stéphane, Torelli, Silvia, Morgan, Jennifer, Muntoni, Francesco, Voit, Thomas, Dumonceaux, JulieVolume:
18
Journal:
Molecular Therapy - Methods & Clinical Development
DOI:
10.1016/j.omtm.2020.06.016
Date:
September, 2020
Fichier:
PDF, 717 KB
2020