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A novel, hybrid, single- and multi-site clinical trial design for CLN3 disease, an ultra-rare lysosomal storage disorder
Adams, Heather R, Defendorf, Sara, Vierhile, Amy, Mink, Jonathan W, Marshall, Frederick J, Augustine, Erika FJournal:
Clinical Trials
DOI:
10.1177/1740774519855715
Date:
June, 2019
Fichier:
PDF, 314 KB
2019