The pro-inflammatory immunophenotype of a Farber disease mouse model is ameliorated by repeated dosing with RVT-801, a developmental enzyme replacement therapy for Farber disease
Sampey, Brante P., Duke, Katie S., Sampey, Gavin C., Gaukel, Eric J., Solyom, Alexander, Wring, Stephen A., He, Xingxuan, Zhu, Changzhi, DeAngelis, Victor, Schuchman, Edward H., Coquery, Christine M.Volume:
126
Langue:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2018.12.329
Date:
February, 2019
Fichier:
PDF, 47 KB
english, 2019