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Intranasal delivery of the CRISPR-Cas9 system for gene editing in MPS II mice
Pimentel, Luisa, Gonzalez, Esteban, Tavares, Angela, Schuh, Roselena, Poletto, Edina, Rodrigues, Graziella, Carneiro, Paola Barcellos, Teixeira, Helder, Giugliani, Roberto, Baldo, GuilhermeVolume:
126
Langue:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2018.12.301
Date:
February, 2019
Fichier:
PDF, 55 KB
english, 2019