Mucopolysaccharidosis type VI enzyme replacement therapy initiated in adulthood: Findings from the MPS VI clinical surveillance program
Harmatz, Paul, Lampe, Christina, Parini, Rossella, Sharma, Reena, Teles, Elisa Leão, Hawley, Sara, Johnson, Julie, Sivam, Debbie, Sisic, ZlatkoVolume:
123
Langue:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2017.12.141
Date:
February, 2018
Fichier:
PDF, 54 KB
english, 2018