AAV-mediated transcription factor EB (TFEB) gene delivery ameliorates muscle pathology and function in the murine model of Pompe Disease
Gatto, Francesca, Rossi, Barbara, Tarallo, Antonietta, Polishchuk, Elena, Polishchuk, Roman, Carrella, Alessandra, Nusco, Edoardo, Alvino, Filomena Grazia, Iacobellis, Francesca, De Leonibus, Elvira,Volume:
7
Langue:
english
Journal:
Scientific Reports
DOI:
10.1038/s41598-017-15352-2
Date:
December, 2017
Fichier:
PDF, 1.69 MB
english, 2017