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Specific factor IX mRNA and protein features favor drug-induced readthrough over recurrent nonsense mutations
Branchini, Alessio, Ferrarese, Mattia, Campioni, Matteo, Castaman, Giancarlo, Mari, Rosella, Bernardi, Francesco, Pinotti, MirkoVolume:
129
Langue:
english
Journal:
Blood
DOI:
10.1182/blood-2016-09-738641
Date:
April, 2017
Fichier:
PDF, 578 KB
english, 2017