714. Gene Therapy Rescues Cone Function and Viability in an Rp2 Knockout Mouse Model for X-Linked Retinitis Pigmentosa Over a Wide Dose Range and a Broad Therapeutic Time Window
Mookherjee, Suddhasil, Hiriyanna, Suja, Kaneshiro, Kayleigh, Qian, Haohua, Li, Tiansen, Khanna, Hemant, Colosi, Peter, Swaroop, Anand, Wu, ZhijianVolume:
23
Langue:
english
Journal:
Molecular Therapy
DOI:
10.1016/s1525-0016(16)34323-4
Date:
May, 2015
Fichier:
PDF, 297 KB
english, 2015