41. Therapeutic Level CRISPR-Oligomer-Mediated Correction of X-CGD Patient Hematopoietic Stem Cells Using Non-Viral, cGMP Compliant, Scalable, and Closed System
Li, Linhong, see De Ravin, Suk, Allen, Cornell, Choi, Uimook, Koontz, Sherry, Theobald, Narda, Lee, Janet, Viley, Angelia, Natarajan, Pachai, NewCombe, Hannah, McMichael, Ashley, Wu, Xiaolin, Malech,Volume:
24
Langue:
english
Journal:
Molecular Therapy
DOI:
10.1016/s1525-0016(16)32850-7
Date:
May, 2016
Fichier:
PDF, 327 KB
english, 2016