Gel-mediated Delivery of AAV1 Vectors Corrects Ventilatory Function in Pompe Mice With Established Disease
Mah, Cathryn S, Falk, Darin J, Germain, Sean A, Kelley, Jeffry S, Lewis, Melissa A, Cloutier, Denise A, DeRuisseau, Lara R, Conlon, Thomas J, Cresawn, Kerry O, Fraites Jr, Thomas J, Campbell-Thompson,Volume:
18
Langue:
english
Journal:
Molecular Therapy
DOI:
10.1038/mt.2009.305
Date:
March, 2010
Fichier:
PDF, 419 KB
english, 2010