Physiological Correction of Pompe Disease by Systemic Delivery of Adeno-associated Virus Serotype 1 Vectors
Mah, Cathryn, Pacak, Christina A, Cresawn, Kerry O, DeRuisseau, Lara R, Germain, Sean, Lewis, Melissa A, Cloutier, Denise A, Fuller, David D, Byrne, Barry JVolume:
15
Langue:
english
Journal:
Molecular Therapy
DOI:
10.1038/sj.mt.6300100
Date:
March, 2007
Fichier:
PDF, 241 KB
english, 2007