A phase 4 prospective study in patients with adult Pompe disease treated with alglucosidase alfa
Thurberg, Beth L., Carlier, Pierre, Kissel, John T., Schoser, Benedikt, Pestronk, Alan, Barohn, Richard, Goker-Alpan, Ozlem, Mozaffar, Tahseen, Pena, Loren D.M., Simmons, Zachary, Straub, Volker, YounVolume:
114
Langue:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2014.12.259
Date:
February, 2015
Fichier:
PDF, 72 KB
english, 2015