SMN2 splice modulators enhance U1–pre-mRNA association and rescue SMA mice
Palacino, James, Swalley, Susanne E, Song, Cheng, Cheung, Atwood K, Shu, Lei, Zhang, Xiaolu, Van Hoosear, Mailin, Shin, Youngah, Chin, Donovan N, Keller, Caroline Gubser, Beibel, Martin, Renaud, NicolVolume:
11
Langue:
english
Journal:
Nature Chemical Biology
DOI:
10.1038/nchembio.1837
Date:
June, 2015
Fichier:
PDF, 1.88 MB
english, 2015