Ataluren (PTC124) Induces Cystic Fibrosis Transmembrane Conductance Regulator Protein Expression and Activity in Children with Nonsense Mutation Cystic Fibrosis
Sermet-Gaudelus, Isabelle, Boeck, Kris De, Casimir, Georges J., Vermeulen, François, Leal, Teresinha, Mogenet, Agnès, Roussel, Delphine, Fritsch, Janine, Hanssens, Laurence, Hirawat, Samit, Miller, NiVolume:
182
Langue:
english
Journal:
American Journal of Respiratory and Critical Care Medicine
DOI:
10.1164/rccm.201001-0137oc
Date:
November, 2010
Fichier:
PDF, 482 KB
english, 2010