Long-term clinical effect and safety of sebelipase alfa in adults with lysosomal acid lipase deficiency
Whitley, Chester B., Valayannopoulos, Vassili, Malinová, Věra, Sharma, Reena, Bourdon, Chris, Boyadjiev, Simeon A., Kessler, Bruce, Twelves, Christopher, Tripuraneni, Radhika, Eckert, Stephen, SchneidVolume:
111
Langue:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2013.12.283
Date:
February, 2014
Fichier:
PDF, 68 KB
english, 2014