Intravenous SBC-103, a recombinant human alpha-N-acetylglucosaminidase reduces CNS heparan sulfate content in a mucopolysaccharidosis type IIIB mouse model
Rutkowski, Joseph V., Harbert, Kari, Xu, Hao, Hu, Wei, Renninger, Matthew, Leavitt, Mark C.C., Chen, Qinming, Rojas-Caro, Sandra, Quinn, Anthony G.Volume:
111
Langue:
english
Journal:
Molecular Genetics and Metabolism
DOI:
10.1016/j.ymgme.2013.12.222
Date:
February, 2014
Fichier:
PDF, 52 KB
english, 2014