RNA Interference Inhibits DUX4-induced Muscle Toxicity In Vivo: Implications for a Targeted FSHD Therapy
Wallace, Lindsay M, Liu, Jian, Domire, Jacqueline S, Garwick-Coppens, Sara E, Guckes, Susan M, Mendell, Jerry R, Flanigan, Kevin M, Harper, Scott Q.Volume:
20
Langue:
english
Journal:
Molecular Therapy
DOI:
10.1038/mt.2012.68
Date:
July, 2012
Fichier:
PDF, 534 KB
english, 2012