Effectiveness of enzyme replacement therapy in 1028 patients with type 1 Gaucher disease after 2 to 5 years of treatment: a report from the Gaucher Registry
Neal J Weinreb, Joel Charrow, Hans C Andersson, Paige Kaplan, Edwin H Kolodny, Pramod Mistry, Gregory Pastores, Barry E Rosenbloom, C.Ronald Scott, Rebecca S Wappner, Ari ZimranVolume:
113
Année:
2002
Langue:
english
DOI:
10.1016/s0002-9343(02)01150-6
Fichier:
PDF, 150 KB
english, 2002