Eliglustat for Gaucher disease Type 1 (GD1): Safety results from a Phase 2 study after 2 years of treatment
M. Judith Peterschmitt, Elena Lukina, Nora Watman, Marta Dragosky, Marcelo Iastrebner, Gregory Pastores, Elsa Avila Arreguin, Hanna Rosenbaum, Mici Phillips, Mathilde Kaper, Dominique Bertin-Millet, AVolume:
102
Année:
2011
Langue:
english
DOI:
10.1016/j.ymgme.2010.11.118
Fichier:
PDF, 58 KB
english, 2011