Human recombinant palmitoyl-protein thioesterase-1 (PPT1) for preclinical evaluation of enzyme replacement therapy for infantile neuronal ceroid lipofuscinosis
Jui-Yun Lu, Jie Hu, Sandra L. HofmannVolume:
99
Année:
2010
Langue:
english
DOI:
10.1016/j.ymgme.2009.12.002
Fichier:
PDF, 405 KB
english, 2010