89. Progression of organ manifestations upon enzyme replacement therapy in a patient with mucopolysaccharidosis type IH prior to hematopoietic stem cell transplantation
Saadet Mercimek-Mahmutoglu, Yolanda Lillquist, Jeff Davis, Christopher Reilly, Derek Human, Paula J. Waters, Eduard Paschke, Lorne A. Clarke, Sylvia Stoeckler-IpsirogluVolume:
96
Année:
2009
Langue:
english
DOI:
10.1016/j.ymgme.2008.11.090
Fichier:
PDF, 42 KB
english, 2009